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Progress and Prospects: Gene Therapy Clinical Trials (Part 2)

Gene Therapy volume 14, pages 1555–1563 (2007)Cite this article

A Corrigendum to this article was published on 04 December 2007

Abstract

This is the second part of a review summarizing progress and prospects in gene therapy clinical research. Twenty key diseases/strategies are succinctly described and commented on by leaders in the field. This part includes clinical trials for skin diseases, neurological disorders, HIV/AIDS, ornithine transcarbamylase deficiency, α1-antitrypsin deficiency, haemophilia and cancer.

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Authors and Affiliations

  1. Department of Gene Therapy, Emmanuel kaye Building, NHLI, Imperial College, Manresa Road, London, UK

    U Griesenbach

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Correspondence to U Griesenbach.

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Eric Alton, Stefano Ferrari and Uta Griesenbach (Progress and Prospects Series Editors)

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Griesenbach, U. Progress and Prospects: Gene Therapy Clinical Trials (Part 2). Gene Ther 14, 1555–1563 (2007). https://doi.org/10.1038/sj.gt.3303033

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