RNA interference: From gene silencing to gene-specific therapeutics
Keywords
RNAi
siRNA
shRNA
Disease
Validation
Therapy
Abbreviations
AAV
adeno-associated virus
ABCA1
ATP-binding cassette, subfamily A, member 1
Bcl-2
B-cell chronic lymphocytic leukemia/lymphoma 2
BCR-ABL
breakpoint cluster region-protooncogene tyrosine-protein kinase ABL1 fusion protein
BMP4
bone morphogenetic protein 4
bp
base pairs
B-RAF
murine sarcoma viral (v-raf) oncogene homolog B1 oncogene
CCR5
chemokine (C–C motif) receptor 5
CD8
T-lymphocyte differentiation antigen T8/Leu-2
CML
chronic myelogenous leukemia
COPD
chronic obstructive pulmonary disease
Cre
causes recombination
CXCR4
chemokine (C–X–C motif), receptor 4
dsRNA
double-stranded RNA
EC
endothelial cell
EGFR
epidermal growth factor receptor
EpCAM
tumour-associated calcium signal transducer 1
ERK
extracellular signal regulated protein kinase
Fas
tumour necrosis factor receptor superfamily, member 6
HBV
hepatitis B virus
HCV
hepatitis C virus
HIV
human immunodeficiency virus
HMG-CoA
beta-hydroxy-beta-methylglutaryl coenzyme A
IFN
interferon
KC
keratinocyte-derived chemokine
K-Ras
c-Kirsten-ras protein
LacZ
β-galactosidase α-peptide
LNA
locked nucleic acid
LoxP
locus χ of crossover P1
LPS
lipopolysaccharide
MAPK
mitogen-activated protein kinase
MDR
multidrug-resistance protein
MIP2
macrophage inflammatory protein-2
miRNA
microRNAs
NF-κB
Nuclear factor-kappaB
PEG
polyethylene glycol
PEI
polyethyleneimine
PKR
dsRNA-dependent protein kinase
RasGAP
Ras GTPase-activating protein
RdDM
RNA-directed DNA methylation
RISC
RNA-induced silencing complex
RNAi
RNA interference
Rnase III
ribonuclease III
RSV
respiratory syncytial virus
SARS
severe acute respiratory syndrome
SCID
severe combined immunodeficiency
shRNA
short hairpin RNA
siRNA
small interfering RNA
S1P
sphingosine 1-phosphate
smad 1
mothers against decapentaplegic homolog 1
smad 7
mothers against decapentaplegic homolog 7
TGFα
transforming growth factor α
TGFβ
transforming growth factor β
TLR3
toll-like receptor 3
TNFα
tumour necrosis factor α
VEGF
vascular endothelial growth factor
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Copyright © 2005 Elsevier Inc. All rights reserved.